Carola J. Maturana, Jessica L. Verpeut, Esteban A. Engel
Current Protocols, May 2022, Wiley
Adeno-associated virus (AAV) vectors have emerged as a potent tool to deliver genes in research and for clinical treatment via gene therapy. We describe a method to measure the number of…
Gene Therapy for Neurological Disorders Europe
11 – 13 July, 2022 | Paris, France
With systemic toxicity challenges plaguing the AAV field, low-dose CNS indications are an ideal target for gene therapy. The plethora of neurological indications dominating gene therapy pipelines…
Next Generation Gene Therapy Vectors
July 18-20, 2022 I Boston, MA
The 2nd Annual Next Generation Gene Therapy Vectors Summit is dedicated to overcoming the current immunogenicity, toxicity and manufacturability challenges facing the field by pioneering the next generation of…
Gene Therapy for Rare Disorders 2022
March 7-10, 2022 I Boston, MAGene Therapy for Rare Disorders is dedicated to overcoming the unique drug development challenges encountered in transforming gene therapy concepts into reality for rare disease patients in need.
As the…
